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TERAPIA CELLULARE

PER LE SARCOGLICANOPATIE


Transplantation of genetically corrected human iPSC-derived progenitors in mice with limb-girdle muscular dystrophy

| Terapia Cellulare

Sci Transl Med . 2012 Jun 27;4(140):140ra89. doi: 10.1126/scitranslmed.3003541.

Francesco Saverio Tedesco 1, Mattia F M Gerli, Laura Perani, Sara Benedetti, Federica Ungaro, Marco Cassano, Stefania Antonini, Enrico Tagliafico, Valentina Artusi, Emanuela Longa, Rossana Tonlorenzi, Martina Ragazzi, Giorgia Calderazzi, Hidetoshi Hoshiya, Ornella Cappellari, Marina Mora, Benedikt Schoser, Peter Schneiderat, Mitsuo Oshimura, Roberto Bottinelli, Maurilio Sampaolesi, Yvan Torrente, Vania Broccoli, Giulio Cossu


Affiliations expand
PMID: 22745439 DOI: 10.1126/scitranslmed.3003541

https://pubmed.ncbi.nlm.nih.gov/22745439/